LGMD2E OR LGMDR4
In 2018 the first clinical trial of gene therapy for LGMD2E or LGMDR4 started in the United States.
Gene Delivery Clinical Trial of SRP-9003 for Patients With LGMD2E (Beta-sarcoglycan Deficiency)
LGMD2D OR LGMDR3
On 2013 a gene therapy clinical trial for LGMD2D or LGMDR3 started in the United States carried out by dr. Jerry Mendell.
Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA
LGMD2C OR LGMDR5
In 2011, a gene therapy clinical trial was carried out in France for LGMD2C or LGMDR5 by dr. Serge Herson.
Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
LGMD2D OR LGMDR3
On 2007, a gene therapy clinical trial was carried out in the United States by Dr. Jerry Mendell
15 October 2020 | Clinical trials
SRP-9003 Gene Therapy for LGMD2E Shows Benefit after 1 year - Muscular Dystrophy News Today - June 9 2020
https://musculardystrophynews.com/2020/06/09/srp-9003-gene-therapy-continues-significant-benefits-children-lgmd2e-phase-1-2-trial/?fbclid=IwAR14O20MUNtLs2wuIwz2oH4CVZivqhmP4IC3ExbKXsZmJXr1H3n6C9Fd4MY
New data gives hope for Limb Girdle Muscular Dystrophy gene therapy - Patient Worthy - June 17, 2020
https://patientworthy.com/2020/06/17/data-gives-hope-limb-girdle-muscular-dystrophy/
31 December 2019 | Clinical trials
SRP-9003 gene therapy shows "very encouraging" results at 9 months in girdle dystrophy - Sarepta Reports - october 9 2019
https://musculardystrophynews.com/2019/10/09/srp-9003-lgmd-2e-gene-therapy-shows-encouraging-9-month-results-sarepta-reports/?fbclid=IwAR2eeni-mgYqgcTPkfFT8aTXsRg6I0WAymm6OENZvBM098ozSKo70btfZ3Q
Myonexus Therapeutics announced the initiation of a trial for the first-ever Gene Therapy for Beta-Sarcoglycanopathy
https://www.businesswire.com/news/home/20181108005462/en/Myonexus-Therapeutics-Announces-Initiation-Trial-First-Ever-Gene?fbclid=IwAR2PCw6Z4WCD2WCJjuD9MwrIbHaysdXpd-WfVZzy5Kt3Mdz9QO2Q7vugv2k
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